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EXP002475

Paper

Dual Strategies Based on Golgi Apparatus/Endoplasmic Reticulum Targeting and Anchoring for High-Efficiency siRNA Delivery and Tumor RNAi Therapy (2025)

Peptide

KDEL-grafted chondroitin sulfate CPD/siBcl-2/CK

Sequence: KDEL

RNA

siRNA

All experiment fields

Experiment Id EXP002475
Paper Dual Strategies Based on Golgi Apparatus/Endoplasmic Reticulum Targeting and Anchoring for High-Effi
Peptide KDEL-grafted chondroitin sulfate CPD/siBcl-2/CK
Delivery Success Class yes
In Vivo Flag yes
Uptake Confirmed yes
Label Confidence high
In Vitro Functional Effect
Endosomal Escape Evidence yes
Peptide Concentration KDEL grafting ratio on chondroitin sulfate approximately 11%
Rna Concentration In vivo siRNA dose 1 mg/kg where applicable; exact in vitro siRNA concentration not fully specified for luciferase assay
Mixing Ratio CPD/siRNA/CK prepared by CPD/siRNA complexation followed by coating with KDEL-grafted chondroitin sulfate; C/Gu ratios screened, same strategy as CPD/siRNA/CS
Formulation Format polymer/polysaccharide nanocomplex
Formulation Components Cell-penetrating poly(disulfide) (CPD), siRNA, KDEL-grafted chondroitin sulfate (CK); CK provides CD44-associated targeting/Golgi transport and KDEL-mediated ER-directed sorting
Size Nm 167.20
Zeta Mv -13.60
Model Scope in_vivo
Model Type in vivo reporter RNAi assay
Cell Lines Or Primary Cells B16F10-Luc melanoma cells
Animal Model C57BL/6 mice bearing subcutaneous B16F10-Luc tumors
Administration Route intravenous injection; every 2 days for 3 doses
Output Type in vivo reporter knockdown
Output Value Tumor luciferase expression reduced to 33.7 ± 5.7%, significantly lower than CPD/siLuc/CS at 54.1 ± 16.2%
Output Units
Output Notes Functional in vivo reporter knockdown qualifies as delivery_success_class = 1. Cy5-siNC biodistribution showed tumor accumulation, and frozen tumor sections confirmed intratumoral fluorescence.
Toxicity Notes No major organ abnormalities reported in HE staining; blood routine and biochemical markers did not show major treatment-related abnormalities.
Curation Notes