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EXP001253

Paper

The endosomal escape vehicle platform enhances delivery of oligonucleotides in preclinical models of neuromuscular disorders (2023)

Peptide

EEV2

Sequence: EEV1-derived cyclic CPP + SV40 NLS (PKKKRKV); full sequence not disclosed

RNA

PMO (antisense oligonucleotide)

All experiment fields

Experiment Id EXP001253
Paper The endosomal escape vehicle platform enhances delivery of oligonucleotides in preclinical models of
Peptide EEV2
Delivery Success Class no
In Vivo Flag no
Uptake Confirmed yes
Label Confidence high
In Vitro Functional Effect yes
Endosomal Escape Evidence
Peptide Concentration
Rna Concentration 2 µM (PMO equiv; LSR-labeled comparator study)
Mixing Ratio
Formulation Format covalent peptide–PMO conjugate
Formulation Components EEV2-PMO654 (± lissamine rhodamine B label in uptake/EGFP assays)
Size Nm
Zeta Mv
Model Scope in_vitro
Model Type in vitro
Cell Lines Or Primary Cells HeLa EGFP-654 cells
Animal Model
Administration Route
Output Type reporter expression
Output Value ~19× higher EGFP fluorescence vs unconjugated PMO; ~9× vs EEV1-PMO654 (at 2 µM, LSR-labeled)
Output Units
Output Notes EGFP fluorescence by flow cytometry and microscopy; uptake quantified via LSR signal.
Toxicity Notes
Curation Notes