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EXP001414

Paper

Calcium condensed cell penetrating peptide complexes offer highly efficient, low toxicity gene silencing (2012)

Peptide

dTAT (double TAT)

Sequence: RKKRRQRRRHRRKKR

RNA

siRNA

All experiment fields

Experiment Id EXP001414
Paper Calcium condensed cell penetrating peptide complexes offer highly efficient, low toxicity gene silen
Peptide dTAT (double TAT)
Delivery Success Class no
In Vivo Flag yes
Uptake Confirmed no
Label Confidence high
In Vitro Functional Effect
Endosomal Escape Evidence
Peptide Concentration dTAT dose escalation up to 1000 mg/kg (tail vein); formulation stock 174 mg/mL dTAT then serial dilution
Rna Concentration Very low siRNA to enable complex formation (final ~0–9.46 nM per 200 µL injection; not intended as therapeutic dose)
Mixing Ratio dTAT + control siRNA + CaCl2 (0.3 M stock; final ~70 mM) + glucose (2%)
Formulation Format Calcium-condensed CPP/siRNA nanoparticles (IV)
Formulation Components dTAT + control siRNA + CaCl2 + glucose
Size Nm
Zeta Mv
Model Scope in_vivo
Model Type in vivo
Cell Lines Or Primary Cells
Animal Model Balb/C mice (male; ~12 weeks) dose-escalation toxicity study
Administration Route Intravenous (tail vein)
Output Type Acute toxicity / behavior after IV dosing
Output Value
Output Units
Output Notes Minimal toxicity observed up to 1000 mg/kg dTAT; highest dose caused transient behavioral phenotype with full recovery.
Toxicity Notes Primary outcome of this arm; no lethal toxicity reported within tested range.
Curation Notes