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EXP001415

Paper

Calcium condensed cell penetrating peptide complexes offer highly efficient, low toxicity gene silencing (2012)

Peptide

dTAT (double TAT)

Sequence: RKKRRQRRRHRRKKR

RNA

siRNA

All experiment fields

Experiment Id EXP001415
Paper Calcium condensed cell penetrating peptide complexes offer highly efficient, low toxicity gene silen
Peptide dTAT (double TAT)
Delivery Success Class yes
In Vivo Flag yes
Uptake Confirmed no
Label Confidence high
In Vitro Functional Effect
Endosomal Escape Evidence
Peptide Concentration dTAT 40 mg/mL formulation; injected 200 µL IV (mouse dose depends on body weight; fixed formulation per group)
Rna Concentration 38.5 µM or 77 µM siRNA in injection formulation (200 µL IV); tissues analyzed at 48 h
Mixing Ratio dTAT + GAPDH siRNA + CaCl2 (final ~70 mM) + glucose (2%)
Formulation Format Calcium-condensed CPP/siRNA nanoparticles (IV)
Formulation Components dTAT + GAPDH siRNA + CaCl2 + glucose
Size Nm 251.00
Zeta Mv
Model Scope in_vivo
Model Type in vivo
Cell Lines Or Primary Cells
Animal Model Balb/C mice (male; 8–12 weeks); tissues: brain, liver, kidney, lung, muscle, stomach
Administration Route Intravenous (tail vein)
Output Type In vivo mRNA knockdown (GAPDH mRNA by qRT-PCR) and siRNA biodistribution (qRT-PCR of siRNA)
Output Value
Output Units
Output Notes Significant GAPDH mRNA knockdown observed especially in lung (both doses), and at higher dose also in muscle and stomach; some knockdown in liver reported. siRNA accumulation highest in lung; dose-dependent.
Toxicity Notes Dose-escalation arm suggests high tolerability of dTAT complexes; no major acute toxicity reported for knockdown/biodistribution dosing.
Curation Notes