Back to browse

EXP001673

Paper

Tat-Conjugated PAMAM Dendrimers as Delivery Agents for Antisense and siRNA Oligonucleotides (2005)

Peptide

Tat-PAMAM G5 dendrimer (BPT)

Sequence: RKKRRQRRRPPQGGC

RNA

antisense oligonucleotide

All experiment fields

Experiment Id EXP001673
Paper Tat-Conjugated PAMAM Dendrimers as Delivery Agents for Antisense and siRNA Oligonucleotides
Peptide Tat-PAMAM G5 dendrimer (BPT)
Delivery Success Class no
In Vivo Flag no
Uptake Confirmed yes
Label Confidence high
In Vitro Functional Effect yes
Endosomal Escape Evidence no
Peptide Concentration Dendrimer (BPT) 10–80 µg/mL used for complexation; functional assays emphasized 10–30 µg/mL (4 h transfection)
Rna Concentration 100 nM oligonucleotide (antisense or siRNA) in Opti-MEM for complex formation and cell treatment
Mixing Ratio Charge ratio (positive/negative) for BPT: antisense 8.7–69.7; siRNA 4.9–38.9 (varied with dendrimer dose 10–80 µg/mL)
Formulation Format Electrostatic dendrimer/oligonucleotide complexes (20 min complexation in Opti-MEM)
Formulation Components BODIPY-labeled PAMAM G5 dendrimer conjugated with Tat (BPT) + oligonucleotide (antisense or siRNA)
Size Nm
Zeta Mv
Model Scope in_vitro
Model Type in vitro
Cell Lines Or Primary Cells NIH 3T3 MDR cells (mouse 3T3 stably expressing human MDR1/P-gp)
Animal Model
Administration Route
Output Type MDR1 functional inhibition (P-glycoprotein expression)
Output Value Partial inhibition of P-glycoprotein expression in viable NIH 3T3 MDR cells at nontoxic dendrimer levels (less effective than Lipofectamine 2000 at low doses).
Output Units
Output Notes Confocal imaging (24 h) showed antisense delivered but largely in intracellular vesicles; only a small fraction released from complexes. Tat conjugation did not improve functional delivery vs unconjugated PAMAM.
Toxicity Notes Dose-dependent toxicity: BPT complexes ~50% cytotoxic at 30 µg/mL with 100 nM oligo; low toxicity (~10–20%) at 10 µg/mL.
Curation Notes