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EXP001692

Paper

Liquid Crystalline Nanodispersions Functionalized with Cell-Penetrating Peptides for Topical Delivery of Short-Interfering RNAs: A Proposal for Silencing a Pro-Inflammatory Cytokine in Cutaneous Diseases (2016)

Peptide

Penetratin (PNT)

Sequence: RQIKIWFQNRRMKWKK (penetratin; as purchased; Antennapedia-derived)

RNA

siRNA (FAM-labeled)

All experiment fields

Experiment Id EXP001692
Paper Liquid Crystalline Nanodispersions Functionalized with Cell-Penetrating Peptides for Topical Deliver
Peptide Penetratin (PNT)
Delivery Success Class no
In Vivo Flag no
Uptake Confirmed yes
Label Confidence high
In Vitro Functional Effect no
Endosomal Escape Evidence
Peptide Concentration 0.025 mM (final) in nanodispersions for characterization/uptake
Rna Concentration 10 µM siRNA in formulations/solutions
Mixing Ratio CPP pre-complexed with siRNA 30 min, then incorporated into nanodispersion; (molar ratio ~2.5:1 CPP:siRNA)
Formulation Format Hexagonal liquid crystalline nanodispersion (monoolein/oleic acid) with PEI, functionalized with CPP
Formulation Components MO:OA:PEI:aqueous phase (8:2:1:89, w/w/w/w) + Poloxamer 407 (1.5%) in Tris-HCl pH 6.5; + PNT + siRNA
Size Nm 294.00
Zeta Mv 15.50
Model Scope in_vitro
Model Type in vitro
Cell Lines Or Primary Cells L929 fibroblasts (24 h uptake study)
Animal Model
Administration Route
Output Type uptake (flow cytometry + fluorescence microscopy)
Output Value High uptake for MO:OA:PEI systems; PNT functionalization improved uptake intensity vs no-CPP but less than TAT.
Output Units
Output Notes Authors selected TAT-functionalized MO:OA:PEI for subsequent in vivo work due to higher uptake intensity.
Toxicity Notes MO:OA:PEI formulations were non-cytotoxic vs untreated L929; OAM-containing systems reduced viability.
Curation Notes