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EXP001693

Paper

Liquid Crystalline Nanodispersions Functionalized with Cell-Penetrating Peptides for Topical Delivery of Short-Interfering RNAs: A Proposal for Silencing a Pro-Inflammatory Cytokine in Cutaneous Diseases (2016)

Peptide

TAT (HIV-1 Tat 47–57)

Sequence: YGRKKRRQRRR

RNA

siRNA

All experiment fields

Experiment Id EXP001693
Paper Liquid Crystalline Nanodispersions Functionalized with Cell-Penetrating Peptides for Topical Deliver
Peptide TAT (HIV-1 Tat 47–57)
Delivery Success Class yes
In Vivo Flag yes
Uptake Confirmed yes
Label Confidence high
In Vitro Functional Effect
Endosomal Escape Evidence
Peptide Concentration 0.1 mM (in nanodispersion)
Rna Concentration 10 µM siRNA TNF-α in topical formulation (100 µL applied)
Mixing Ratio CPP pre-complexed with siRNA 30 min, then added to nanodispersion
Formulation Format Topical hexagonal liquid crystalline nanodispersion (MO:OA:PEI) functionalized with TAT
Formulation Components MO:OA:PEI:aqueous phase (8:2:1:89, w/w/w/w) + Poloxamer 407 (1.5%) + TAT + siRNA TNF-α
Size Nm 310.00
Zeta Mv 12.00
Model Scope in_vivo
Model Type in vivo
Cell Lines Or Primary Cells
Animal Model Hairless mice (HRS/J); TPA-induced cutaneous inflammation model (psoriasis-like)
Administration Route Topical (100 µL over 2 cm² on back skin); TPA applied 1 h later; analysis at 6 h post-TPA
Output Type in vivo functional knockdown (protein level)
Output Value Significant reduction of skin TNF-α levels (ELISA) vs controls; TAT-functionalized nanodispersion outperformed non-functionalized nanodispersion and PEI solution controls.
Output Units
Output Notes In vivo skin penetration also assessed with FAM-siRNA (12 h) showing deeper penetration with TAT-functionalized nanodispersion.
Toxicity Notes No significant skin irritation by H&E (no epidermal thickening/inflammatory infiltration) for MO:OA:PEI ± TAT.
Curation Notes