Back to browse

EXP001774

Paper

Delivery of siRNA to the brain using a combination of nose-to-brain delivery and cell-penetrating peptide-modified nano-micelles (2013)

Peptide

Tat-G (Tat analog)

Sequence: GRKKRRQRRRG (Tat-G: Gly-Arg-Lys-Lys-Arg-Arg-Gln-Arg-Arg-Arg-Gly)

RNA

siRNA (fluorescently labeled for tracking); Alexa-dextran (10 kDa) used as model siRNA

All experiment fields

Experiment Id EXP001774
Paper Delivery of siRNA to the brain using a combination of nose-to-brain delivery and cell-penetrating pe
Peptide Tat-G (Tat analog)
Delivery Success Class no
In Vivo Flag yes
Uptake Confirmed yes
Label Confidence high
In Vitro Functional Effect
Endosomal Escape Evidence
Peptide Concentration
Rna Concentration 0.5 mg/mL FAM-siRNA for intranasal dosing (80 µL total; reported dose 40 µg)
Mixing Ratio N/P = 20 used for in vivo studies (complexation tested N/P 1–30)
Formulation Format CPP-modified PEG-PCL polymeric nano-micelle / polyion complex
Formulation Components MPEGePCLeTat (PEG-PCL copolymer conjugated to Tat-G) complexed with siRNA (or Alexa-dextran model)
Size Nm 50.00
Zeta Mv 10.00
Model Scope in_vivo
Model Type in vivo
Cell Lines Or Primary Cells
Animal Model Sprague–Dawley male rats, 8-week old
Administration Route Intranasal (80 µL total over 30 min; 5–10 µL drops every 2–3 min); comparator: IV tail vein (100 µL)
Output Type Brain/olfactory bulb delivery (fluorescence quantification & imaging)
Output Value Intranasal delivery produced significantly higher brain levels than IV; Tat-micelles increased brain/olfactory bulb and trigeminal nerve/CSF signal vs naked
Output Units
Output Notes Primarily distribution/transport study via olfactory and trigeminal pathways (FAM-siRNA & Alexa-dextran tracer). No in vivo gene knockdown/phenotype shown.
Toxicity Notes No apparent toxicity discussed in this paper for the intranasal siRNA study
Curation Notes