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EXP002464

Paper

Intraocular siRNA Delivery Mediated by Penetratin Derivative to Silence Orthotopic Retinoblastoma Gene (2023)

Peptide

89WP (penetratin derivative)

Sequence: RQIKIWFWWRRMKWKK

RNA

siRNA

All experiment fields

Experiment Id EXP002464
Paper Intraocular siRNA Delivery Mediated by Penetratin Derivative to Silence Orthotopic Retinoblastoma Ge
Peptide 89WP (penetratin derivative)
Delivery Success Class no
In Vivo Flag no
Uptake Confirmed yes
Label Confidence high
In Vitro Functional Effect yes
Endosomal Escape Evidence
Peptide Concentration Defined via charge ratio
Rna Concentration 1 µg/mL siRNA (in vitro)
Mixing Ratio PA N/P=2:1; 89WP:siRNA=15:1 (optimized)
Formulation Format siRNA/PA/89WP polyplex
Formulation Components siRNA + PAMAM G3 + 89WP
Size Nm 60.00
Zeta Mv 20.00
Model Scope in_vitro
Model Type in vitro
Cell Lines Or Primary Cells ARPE-19; WERI-Rb-1-luci
Animal Model
Administration Route
Output Type Gene silencing (luciferase)
Output Value Near-complete luciferase knockdown vs naked siRNA
Output Units
Output Notes Confocal, flow cytometry uptake; functional silencing without chloroquine
Toxicity Notes Cell viability >80%
Curation Notes