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Sustained Dystrophin Expression Induced by Peptide-conjugated Morpholino Oligomers in the Muscles of mdx Mice
Paper ID
PAPER000197
Year
2008
DOI
10.1038/mt.2008.120
PMID
18545222
Journal
Molecular Therapy
Source URL
Experiments
EXP001123
with
CPP-A (PPMO-A)
(ASO)
EXP001124
with
CPP-B (PPMO-B)
(ASO)
EXP001125
with
CPP-C (PPMO-C)
(ASO)
EXP001126
with
CPP-D (PPMO-D)
(ASO)
EXP001127
with
CPP-E (PPMO-E)
(ASO)
EXP001128
with
CPP-F (PPMO-F)
(ASO)
EXP001129
with
CPP-G (PPMO-G)
(ASO)
EXP001130
with
CPP-H (PPMO-H)
(ASO)
EXP001131
with
CPP-I (PPMO-I)
(ASO)
EXP001132
with
CPP-J (PPMO-J)
(ASO)
EXP001133
with
CPP-K (PPMO-K)
(ASO)
EXP001134
with
CPP-L (PPMO-L)
(ASO)
EXP001135
with
CPP-M (PPMO-M)
(ASO)
EXP001136
with
CPP-N (PPMO-N)
(ASO)
EXP001137
with
CPP-B conjugate (M23D-B, dystrophin-targeting PPMO)
(ASO)
EXP001138
with
CPP-B conjugate (mis-23D-B, mismatched PMO control)
(ASO)