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Cell-penetrating peptide-conjugated, splice-switching oligonucleotides mitigate the phenotype in Btk/Tec double deficient X-linked agammaglobulinemia model
Paper ID
PAPER000493
Year
2025
DOI
10.1039/d4cb00312h
PMID
Journal
RSC Chemical Biology
Source URL
Experiments
EXP002441
with
Pip6a-PMO 186
(SCO)
EXP002442
with
B-PMO 186
(SCO)
EXP002443
with
Pip6a-PMO 186
(SCO)
EXP002444
with
Pip6a-PMO 186
(SCO)
EXP002445
with
Pip6a-PMO 186
(SCO)