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Amphiphilic lipopeptide significantly enhances uptake of charge-neutral splice switching morpholino oligonucleotide in spinal muscular atrophy patient-derived fibroblasts
- Paper ID
- PAPER000166
- Year
- 2017
- DOI
- 10.1016/j.ijpharm.2017.08.116
- PMID
- 28864392
- Journal
- International Journal of Pharmaceutics
- Source URL
-
Experiments