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Amphiphilic lipopeptide significantly enhances uptake of charge-neutral splice switching morpholino oligonucleotide in spinal muscular atrophy patient-derived fibroblasts

Paper ID
PAPER000166
Year
2017
DOI
10.1016/j.ijpharm.2017.08.116
PMID
28864392
Journal
International Journal of Pharmaceutics
Source URL

Experiments