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Peptide-conjugated antimiRs improve myotonic dystrophy type 1 phenotypes by promoting endogenous MBNL1 expression
- Paper ID
- PAPER000189
- Year
- 2023
- DOI
- 10.1016/j.omtn.2023.09.001
- PMID
- 37744174
- Journal
- Molecular Therapy Nucleic Acids
- Source URL
-
Experiments