A peptide conjugate enables systemic injection of the morpholino inducer and more durable induction of T3H38 ribozyme-controlled AAV transgene in mice

Paper ID: PAPER000380
Year: 2025
DOI: 10.1038/s41434-025-00519-8
PMID: 39939797
Journal: Gene Therapy
Source URL

Experiments

EXP002162 with v-M8 (morpholino oligonucleotide (PMO))
EXP002163 with B-M8 (morpholino oligonucleotide (PMO))
EXP002164 with B-MSP-M8 (morpholino oligonucleotide (PMO))