SCO

Linked experiment: EXP000515

Linked peptide: BPP12

Linked paper: Efficient systemic CNS delivery of a therapeutic antisense oligonucleotide with a blood-brain barrier-penetrating ApoE-derived peptide (2024)

RNA overview

RNA Type: SCO
Payload/target: SMN2 exon-7 inclusion
Target gene/transcript: not reported

Sequence information

Sequence reported in source article: no
RNA sequence: not reported
Sense strand
Antisense strand

Chemical modifications

RNA modifications: Cy7-labelled PMO in biodistribution studies