ASO

Linked experiment: EXP001179

Linked peptide: EEV2

Linked paper: The endosomal escape vehicle platform enhances delivery of oligonucleotides in preclinical models of neuromuscular disorders (2023)

RNA overview

RNA Type: ASO
Payload/target: PMO-PAS (targets DUX4 polyadenylation signal; FSHD)
Target gene/transcript: not reported

Sequence information

Sequence reported in source article: no
RNA sequence: not reported
Sense strand
Antisense strand

Chemical modifications

RNA modifications: phosphorodiamidate morpholino oligomer