ASO

Linked experiment: EXP002198

Linked peptide: Peptide B

Linked paper: Systemic delivery of a peptide-linked morpholino oligonucleotide neutralizes mutant RNA toxicity in a mouse model of myotonic dystrophy (2013)

RNA overview

RNA Type: ASO
Payload/target: CAG25 morpholino targeting CUG repeat RNA (DMPK)
Target gene/transcript: CUG repeat

Sequence information

Sequence reported in source article: no
RNA sequence: not reported
Sense strand
Antisense strand

Chemical modifications

RNA modifications: morpholino chemistry; peptide conjugated at 5′ end