ASO

Linked experiment: EXP002212

Linked peptide: RC-1001 CPP (proprietary)

Linked paper: A cell-penetrating peptide enhances delivery and efficacy of phosphorodiamidate morpholino oligomers in mdx mice (2022)

RNA overview

RNA Type: ASO
Payload/target: Dmd exon 23 (exon skipping)
Target gene/transcript: not reported

Sequence information

Sequence reported in source article: no
RNA sequence: not reported
Sense strand
Antisense strand

Chemical modifications

RNA modifications: phosphorodiamidate morpholino oligomer