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ASO (PMO)

Linked experiment: EXP000258

Linked peptide: H4-ApoE(141–150)

Linked paper: Endosomal escape cell-penetrating peptides significantly enhance pharmacological effectiveness and CNS activity of systemically administered antisense oligonucleotides (2021)

RNA fields

RNA Type
ASO (PMO)
RNA Payload Or Target
SMN2 exon-7 splice correction
RNA Modifications
Phosphorodiamidate morpholino