Back to browse

PMO (phosphorodiamidate morpholino oligonucleotide; splice-switching)

Linked experiment: EXP000999

Linked peptide: PF6

Linked paper: Peptide Nanoparticle Delivery of Charge-Neutral Splice-Switching Morpholino Oligonucleotides (2015)

RNA fields

RNA Type
PMO (phosphorodiamidate morpholino oligonucleotide; splice-switching)
RNA Payload Or Target
PMO XLA (BTK intron reporter splice correction); 5'-CTACAGAGTTCTCAGGATGTAAGCA-3'
RNA Modifications
PMO (charge-neutral morpholino backbone; steric-block splice-switching oligo)