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PMO (phosphorodiamidate morpholino oligonucleotide; splice-switching)

Linked experiment: EXP001002

Linked peptide: PF14

Linked paper: Peptide Nanoparticle Delivery of Charge-Neutral Splice-Switching Morpholino Oligonucleotides (2015)

RNA fields

RNA Type
PMO (phosphorodiamidate morpholino oligonucleotide; splice-switching)
RNA Payload Or Target
PMO SMA 18-mer (ISS-N1); 5'-TCACTTTCATAATGCTGG-3'; PMO SMA 20-mer (ISS-N1); 5'-ATTCACTTTCATAATGCTGG-3'; PMO SMA 23-mer (ISS-N1); 5'-ATTCACTTTCATAATGCTGGCAG-3'; PMO SMA 25-mer (ISS-N1); 5'-AGATTCACTTTCATAATGCTGGCAG-3'
RNA Modifications
PMO (charge-neutral morpholino backbone; steric-block splice-switching oligo)