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PMO (phosphorodiamidate morpholino oligonucleotide; splice-switching)

Linked experiment: EXP001013

Linked peptide: Pal-RXR4

Linked paper: Peptide Nanoparticle Delivery of Charge-Neutral Splice-Switching Morpholino Oligonucleotides (2015)

RNA fields

RNA Type
PMO (phosphorodiamidate morpholino oligonucleotide; splice-switching)
RNA Payload Or Target
PMO DMD (M23D; exon 23 skipping); 5'-GGCCAAACCTCGGCTTACCTGAAAT-3'
RNA Modifications
PMO (charge-neutral morpholino backbone; steric-block splice-switching oligo)