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PMO (antisense oligonucleotide)

Linked experiment: EXP001257

Linked peptide: EEV1

Linked paper: The endosomal escape vehicle platform enhances delivery of oligonucleotides in preclinical models of neuromuscular disorders (2023)

RNA fields

RNA Type
PMO (antisense oligonucleotide)
RNA Payload Or Target
PMO-23 (induces murine Dmd exon 23 skipping)
RNA Modifications
phosphorodiamidate morpholino oligomer