PMO (antisense oligonucleotide)

Linked experiment: EXP001262

Linked peptide: EEV2

Linked paper: The endosomal escape vehicle platform enhances delivery of oligonucleotides in preclinical models of neuromuscular disorders (2023)

RNA fields

RNA Type: PMO (antisense oligonucleotide)
RNA Payload Or Target: PMO-PAS (targets DUX4 polyadenylation signal; FSHD)
RNA Modifications: phosphorodiamidate morpholino oligomer