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PNA (steric-blocking)

Linked experiment: EXP001338

Linked peptide: RXR4–PNADMD

Linked paper: Improved cell-penetrating peptide–PNA conjugates for splicing redirection in HeLa cells and exon skipping in mdx mouse muscle (2008)

RNA fields

RNA Type
PNA (steric-blocking)
RNA Payload Or Target
PNADMD targets dystrophin exon 23 region for exon skipping (DMD/mdx model)
RNA Modifications