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PMO (antisense oligonucleotide)

Linked experiment: EXP002368

Linked peptide: RC-1001 CPP (proprietary)

Linked paper: A cell-penetrating peptide enhances delivery and efficacy of phosphorodiamidate morpholino oligomers in mdx mice (2022)

RNA fields

RNA Type
PMO (antisense oligonucleotide)
RNA Payload Or Target
Dmd exon 23 (exon skipping)
RNA Modifications
phosphorodiamidate morpholino oligomer