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EXP001960

Paper

Effective In Vivo Topical Delivery of siRNA and Gene Silencing in Intact Corneal Epithelium Using a Modified Cell-Penetrating Peptide (2019)

Peptide

Chol-POD / siRNA polyplex

Sequence: CGGGARKKAAKAARKKAAKAARKKAAKAARKKAAKA

RNA

siRNA (siGLO; siLuc; NSC4)

All experiment fields

Experiment Id EXP001960
Paper Effective In Vivo Topical Delivery of siRNA and Gene Silencing in Intact Corneal Epithelium Using a
Peptide Chol-POD / siRNA polyplex
Delivery Success Class no
In Vivo Flag no
Uptake Confirmed yes
Label Confidence high
In Vitro Functional Effect no
Endosomal Escape Evidence
Peptide Concentration
Rna Concentration
Mixing Ratio 35:1 (POD:siRNA molar ratio) in PBS; 1 µM siRNA used in most in vitro assays.
Formulation Format Noncovalent CPP–siRNA polyplex
Formulation Components Chol-POD complexed with siRNA in PBS (35:1).
Size Nm 150.80
Zeta Mv 15.60
Model Scope in_vitro
Model Type in vitro
Cell Lines Or Primary Cells HCE-S human corneal epithelial cells
Animal Model
Administration Route
Output Type In vitro uptake (fluorescence microscopy); in vitro luciferase knockdown (dual luciferase assay)
Output Value Uptake observed as punctate perinuclear cytoplasmic fluorescence; no significant luciferase knockdown without endosomal disruptor.
Output Units
Output Notes Authors infer endosomal entrapment because uptake without knockdown; used chloroquine to test escape hypothesis.
Toxicity Notes MTT viability generally ~75–100% at 17.5–35 µM (drops to ~55% at 70 µM for Chol-/Palm-/POD).
Curation Notes