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EXP001972

Paper

Effective In Vivo Topical Delivery of siRNA and Gene Silencing in Intact Corneal Epithelium Using a Modified Cell-Penetrating Peptide (2019)

Peptide

QN-Palm-POD / siLuc topical eye drop (luciferase knockdown)

Sequence: CGGGARKKAAKAARKKAAKAARKKAAKAARKKAAKA

RNA

siRNA

All experiment fields

Experiment Id EXP001972
Paper Effective In Vivo Topical Delivery of siRNA and Gene Silencing in Intact Corneal Epithelium Using a
Peptide QN-Palm-POD / siLuc topical eye drop (luciferase knockdown)
Delivery Success Class yes
In Vivo Flag yes
Uptake Confirmed no
Label Confidence high
In Vitro Functional Effect
Endosomal Escape Evidence yes
Peptide Concentration
Rna Concentration
Mixing Ratio 140:1 (700 µM QN-Palm-POD + 5 µM siRNA) applied daily for 4 days (split-eye design).
Formulation Format CPP–siRNA polyplex with covalent endosomal disruptor (topical ocular delivery)
Formulation Components QN-Palm-POD complexed with siLuc (right eye) vs NSC4 (left eye); luciferase activity monitored in vivo.
Size Nm 107.00
Zeta Mv 14.90
Model Scope in_vivo
Model Type in vivo
Cell Lines Or Primary Cells
Animal Model Mouse Krt12+/luc2 corneal epithelium luciferase reporter model (split-eye control: siLuc vs NSC4)
Administration Route Topical eye drop daily for 4 days (2.5 µL per eye); IVIS luciferase imaging
Output Type In vivo functional RNA delivery (reporter gene silencing)
Output Value Up to ~30% knockdown of corneal luciferase signal (max around day 9; significant after treatment withdrawal).
Output Units
Output Notes Histology and clinical eye exams reported no swelling/edema/inflammation in treated eyes.
Toxicity Notes No corneal abnormalities on H&E; eyes remained 'quiet' by ophthalmic exam during and after treatment.
Curation Notes