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EXP002007

Paper

A blood–brain barrier- and blood–brain tumor barrier-penetrating siRNA delivery system targeting gliomas for brain tumor immunotherapy (2024)

Peptide

Cholesterol-T7-PEG2-DP7 peptide

Sequence: cholesterol-HAIYPRH-PEG2-VQWRIRVAVIRK

RNA

siRNA (Cy5-labeled for biodistribution imaging)

All experiment fields

Experiment Id EXP002007
Paper A blood–brain barrier- and blood–brain tumor barrier-penetrating siRNA delivery system targeting gli
Peptide Cholesterol-T7-PEG2-DP7 peptide
Delivery Success Class no
In Vivo Flag yes
Uptake Confirmed no
Label Confidence medium
In Vitro Functional Effect
Endosomal Escape Evidence
Peptide Concentration
Rna Concentration 1 mg/kg cy5-siRNA i.v.; 4 h biodistribution readout.
Mixing Ratio Peptide:siRNA mass ratio 10:1 (incubated before i.v. administration).
Formulation Format Cholesterol-peptide/siRNA complex (electrostatic)
Formulation Components Cholesterol-T7-PEG2-DP7 peptide complexed with cy5-siRNA for BBB/BBTB penetration screening. PEG2 linker; T7 head.
Size Nm
Zeta Mv
Model Scope in_vivo
Model Type in vivo
Cell Lines Or Primary Cells
Animal Model Normal mice and/or GL261 tumor-bearing mice (biodistribution imaging at 4 h).
Administration Route Intravenous (i.v.) single dose; organs collected at 4 h for IVIS imaging and brain section CLSM.
Output Type In vivo biodistribution: brain fluorescence signal after i.v. administration (BBB/BBTB penetration screening).
Output Value Brain accumulation signal detected; DAT (DP7-ACP-T7) reported as strongest among tested peptide/linker configurations.
Output Units
Output Notes Screening used DP7 and T7 as target heads with different linkers (ACP, PEG2, Gly6) and orientations.
Toxicity Notes
Curation Notes