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Systemic peptide-mediated oligonucleotide therapy improves long-term survival in spinal muscular atrophy
- Paper ID
- PAPER000406
- Year
- 2016
- DOI
- 10.1073/pnas.1605731113
- PMID
- 27621445
- Journal
- Proceedings of the National Academy of Sciences
- Source URL
-
Experiments
-
EXP002295
with
Pip6a
(PMO (splice-switching antisense oligonucleotide))
-
EXP002296
with
Pip6a
(PMO (splice-switching antisense oligonucleotide))