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Systemic delivery of a peptide-linked morpholino oligonucleotide neutralizes mutant RNA toxicity in a mouse model of myotonic dystrophy
- Paper ID
- PAPER000423
- Year
- 2013
- DOI
- 10.1089/nat.2012.0404
- PMID
- 23308382
- Journal
- Nucleic Acid Therapeutics
- Source URL
-
Experiments