ASO

Linked experiment: EXP001137

Linked peptide: CPP-B conjugate (M23D-B, dystrophin-targeting PPMO)

Linked paper: Sustained Dystrophin Expression Induced by Peptide-conjugated Morpholino Oligomers in the Muscles of mdx Mice (2008)

RNA overview

RNA Type: ASO
Payload/target: mouse dystrophin intron 23 5' splice site (exon 23 skipping)
Target gene/transcript: not reported

Sequence information

Sequence reported in source article: yes
RNA sequence: sense:GGCCAAACCTCGGCTTACCTGAAAT
Sense strand: GGCCAAACCTCGGCTTACCTGAAAT
Antisense strand

Chemical modifications

RNA modifications: phosphorodiamidate morpholino oligomer (PMO)