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ASO

Linked experiment: EXP001138

Linked peptide: CPP-B conjugate (mis-23D-B, mismatched PMO control)

Linked paper: Sustained Dystrophin Expression Induced by Peptide-conjugated Morpholino Oligomers in the Muscles of mdx Mice (2008)

RNA overview

RNA Type
ASO
Payload/target
mismatched dystrophin-targeting PMO control (mis-23D-B)
Target gene/transcript
dystrophin

Sequence information

Sequence reported in source article
yes
RNA sequence
sense:GCGCAAACCTCGCGTTACCGTAAAT
Sense strand
GCGCAAACCTCGCGTTACCGTAAAT
Antisense strand

Chemical modifications

RNA modifications
phosphorodiamidate morpholino oligomer (PMO)