PMO

Linked experiment: EXP000534

Linked peptide: BPP8

Linked paper: Efficient systemic CNS delivery of a therapeutic antisense oligonucleotide with a blood-brain barrier-penetrating ApoE-derived peptide (2024)

RNA fields

RNA Type: PMO
RNA Payload Or Target: SMN2 exon-7 inclusion
RNA Modifications: Cy7-labelled PMO in biodistribution studies