Back to browse

antisense oligonucleotide (AON)

Linked experiment: EXP000633

Linked peptide: P1-9R

Linked paper: Erythroid-Progenitor-Targeted Gene Therapy Using Bifunctional TFR1 Ligand-Peptides in Human Erythropoietic Protoporphyria (2019)

RNA fields

RNA Type

antisense oligonucleotide (AON)

RNA Payload Or Target

AON-V1 (FECH intron 3 splice correction)

RNA Modifications

Phosphorothioate AON (as previously reported)