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PMO (morpholino antisense oligo)

Linked experiment: EXP001212

Linked peptide: CPP-B conjugate (M23D-B, dystrophin-targeting PPMO)

Linked paper: Sustained Dystrophin Expression Induced by Peptide-conjugated Morpholino Oligomers in the Muscles of mdx Mice (2008)

RNA fields

RNA Type
PMO (morpholino antisense oligo)
RNA Payload Or Target
mouse dystrophin intron 23 5' splice site (exon 23 skipping)
RNA Modifications
phosphorodiamidate morpholino oligomer (PMO)