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EXP002506

Paper

Multifunctional polyion complex micelle featuring enhanced stability, targetability, and endosome escapability for systemic siRNA delivery to subcutaneous model of lung cancer (2014)

Peptide

cRGD-PEG-PAsp(TEP)-Chol

Sequence: cyclo(RGDfK); main text reports cyclo-RGDfK/cRGD peptide, with N-terminal cysteine used for conjugation

RNA

siRNA

All experiment fields

Experiment Id EXP002506
Paper Multifunctional polyion complex micelle featuring enhanced stability, targetability, and endosome es
Peptide cRGD-PEG-PAsp(TEP)-Chol
Delivery Success Class yes
In Vivo Flag yes
Uptake Confirmed yes
Label Confidence high
In Vitro Functional Effect
Endosomal Escape Evidence
Peptide Concentration
Rna Concentration 25 µg siRNA/mouse/injection; 8 total injections for therapy; 2 injections for qRT-PCR knockdown study
Mixing Ratio N/P = 3
Formulation Format targeted/stabilized polyion complex micelle
Formulation Components cRGD-PEG-PAsp(TEP)-Chol block copolymer complexed with siPlk1; PEG shell, cRGD targeting ligand, PAsp(TEP) cationic/endosome-disrupting segment, cholesteryl stabilizing moiety
Size Nm -50.00
Zeta Mv
Model Scope in_vivo
Model Type in vivo therapeutic gene silencing
Cell Lines Or Primary Cells A549 human lung carcinoma xenograft
Animal Model BALB/c nude mice bearing subcutaneous A549 tumors
Administration Route intravenous tail vein
Output Type tumor growth inhibition and target mRNA knockdown
Output Value significant tumor growth inhibition and ~30% PLK1 mRNA reduction in tumor tissue compared with siScr micelle and buffer controls
Output Units
Output Notes Functional in vivo RNAi was sequence-specific: siPlk1 micelle reduced PLK1 mRNA and inhibited A549 tumor growth, while siScr micelle did not.
Toxicity Notes Negligible liver toxicity: ALT and AST were not significantly different from control after cRGD-PEG-PAsp(TEP)-Chol/siScr micelle administration.
Curation Notes