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EXP002001

Paper

A blood–brain barrier- and blood–brain tumor barrier-penetrating siRNA delivery system targeting gliomas for brain tumor immunotherapy (2024)

Peptide

Cholesterol-DP7-ACP-T7 (DAT) (dual-functional peptide on liposome)

Sequence: cholesterol-VQWRIRVAVIRK-ACP-HAIYPRH

RNA

siRNA (duplex, 21-mer with 3′ TT overhangs)

All experiment fields

Experiment Id EXP002001
Paper A blood–brain barrier- and blood–brain tumor barrier-penetrating siRNA delivery system targeting gli
Peptide Cholesterol-DP7-ACP-T7 (DAT) (dual-functional peptide on liposome)
Delivery Success Class no
In Vivo Flag no
Uptake Confirmed yes
Label Confidence high
In Vitro Functional Effect yes
Endosomal Escape Evidence yes
Peptide Concentration DAT used to modify LNP at 250 μg/mL (chosen as optimal).
Rna Concentration 0.24 μg cy3-siRNA per well (24-well) with 1.44 μg LNP/DAT-LNP (mass ratio 6:1) for uptake/transfection assays; functional assays used DAT-LNP/si slit2 (dose given as 1.2 μg siRNA in migration/invasion pretreatment).
Mixing Ratio DAT-LNP:siRNA mass ratio 6:1 (gel retardation complete at 6:1).
Formulation Format DAT-modified DOTAP:cholesterol liposome (DAT-LNP) electrostatically adsorbing siRNA
Formulation Components DOTAP:cholesterol (1:1 molar; DOTAP 2 mg/mL) liposome + DAT peptide (250 μg/mL for modification; dialysis) + siRNA (complexed at 6:1 mass ratio LNP:siRNA).
Size Nm 130.10
Zeta Mv
Model Scope in_vitro
Model Type in vitro
Cell Lines Or Primary Cells GL261 mouse glioma cells (uptake/transfection, slit2 knockdown, migration/invasion); BV2 microglia (targeting coculture); bEnd.3 brain microvascular endothelial cells (in vitro BBB model); BMDCs/BMDMs (immune modulation assays).
Animal Model
Administration Route
Output Type In vitro uptake + functional RNA effect: siRNA transfection (flow cytometry/microscopy), slit2 mRNA/protein knockdown (RT–PCR/WB), reduced migration/invasion; immune activation (DC maturation, macrophage polarization).
Output Value High transfection of cy3-siRNA in GL261 (flow + microscopy); significant slit2 knockdown; migration/invasion inhibited; DAT-LNP promotes DC maturation and shifts macrophages toward M1 markers (iNOS↑, IL-10↓).
Output Units
Output Notes Uptake pathways: caveolin- and clathrin-mediated endocytosis (CTB/transferrin colocalization; inhibited by genistein/chlorpromazine).
Toxicity Notes DAT-LNP showed slightly lower toxicity vs Lipo2000/LNP in 293T CCK-8 assay (qualitative).
Curation Notes