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antisense morpholino (PPMO)

Linked experiment: EXP002354

Linked peptide: Peptide B

Linked paper: Systemic delivery of a peptide-linked morpholino oligonucleotide neutralizes mutant RNA toxicity in a mouse model of myotonic dystrophy (2013)

RNA fields

RNA Type
antisense morpholino (PPMO)
RNA Payload Or Target
CAG25 morpholino targeting CUG repeat RNA (DMPK)
RNA Modifications
morpholino chemistry; peptide conjugated at 5′ end